Drug that Targets the PDGFRA exon 18/PDGFRA D842V mutation

Blueprint Medicines

CAMBRIDGE, Mass., January 9, 2020 – Blueprint Medicines Corporation (NASDAQ: BPMC), a precision therapy company focused on genomically defined cancers, rare diseases and cancer immunotherapy, today announced that the U.S. Food and Drug Administration (FDA) has approved AYVAKITβ„’ (avapritinib) for the treatment of adults with unresectable or metastatic gastrointestinal stromal tumor (GIST) harboring a platelet-derived growth factor receptor alpha (PDGFRA) exon 18 mutation, including PDGFRA D842V mutations. AYVAKIT is the first precision therapy approved to treat a genomically defined population of patients with GIST.Β  Read more…

See also Blueprint Medicines and Ayvakit (avapritinib) for more information.

Ayvakit (avapritinib)